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March 3, 2026
L-Arginine FOR SCA6: PHASE2 clinical trial in Japan
TI
Tomohiko Ishihara
Niigata University Medical and Dental Hospital
KI
Kensuke Ikenaka
YT
Yuji Takahashi
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Key Points
L-arginine treatment shows promise in improving neurological function in SCA6 patients, indicating meaningful outcomes.
The study reports significant improvements in specific biomarkers related to neurological health among participants.
Phase 2 clinical trial assesses the efficacy of l-arginine in treating a rare genetic neurological disorder called SCA6.
Findings suggest that l-arginine could become a valuable treatment option, though further studies are warranted.
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Ishihara et al. (Mon,) studied this question.
synapsesocial.com/papers/69a75f53c6e9836116a2a9ec
https://doi.org/https://doi.org/10.1016/j.jns.2025.124013
L-Arginine FOR SCA6: PHASE2 clinical trial in Japan | Synapse