Long-term neurological outcome after hematopoietic stem cell transplant in juvenile Krabbe disease

Key Points

• Long-term neurological outcome significantly varies in juvenile Krabbe disease, influencing patient care decisions.
• Children who received hematopoietic stem cell transplant show diverse neurological progress over time.
• Observational analysis highlights neurodevelopment as a critical factor following hematopoietic stem cell transplant.
• Calls for enhanced monitoring and support strategies in managing juvenile Krabbe disease post-transplant.