Motor Function Changes in Duchenne Muscular Dystrophy: A Case Series Using Conventional and Spinal Muscular Atrophy-Based Assessments During Viltolarsen Treatment

Key Points

• Motor function changes indicate potential improvements during viltolarsen treatment.
• Significant assessments of motor function were conducted using both conventional and SMA-based methods.
• The case series presents detailed observations over a specified treatment period involving viltolarsen.
• Further validation in larger cohorts is needed to confirm these findings across various populations.